69 Best Rna Based And Rna Targeted Therapeutics Startups to Watch in 2025

The Definitive Seedtable Ranking of Rna Based And Rna Targeted Therapeutics Startups

We track 71,000+ companies and rank them dynamically using our Seedtable Score – a score that uses quantitative and qualitative data points to signal the momentum behind a company. We then monitor the list manually leveraging our expertise as founders and investors.

There are 80 start-ups with an aggregate funding of $6.9b. The average funding per company in this subset is $99.3m.

Last update to the database: Feb 18, 2025. See changelog.

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Ligandal logo

Ligandal

Nanomedicine company developing vaccines and therapies with cell-specific targeting.

6

Funding Rounds

$4.6m

Money raised

Scipher Medicine logo

Scipher Medicine

Scipher Medicine is a precision immunology company that aims to match patients with their most effective therapy. Their proprietary platform, Spectra, combines AI and a network map of protein interactions in the human body to make predictions.

2

Funding Rounds

$192.0m

Money raised

Talus Bioscience logo

Talus Bioscience

Talus Bioscience is a Seattle-based company founded by Alex Federation.

1

Funding Rounds

$11.2m

Money raised

Translate Bio logo

Translate Bio

Translate Bio is a clinical-stage mRNA therapeutics company developing medicines to treat diseases caused by protein or gene dysfunction and vaccines against infectious disease pathogens.

6

Funding Rounds

$227.7m

Money raised

ProNAi Therapeutics logo

ProNAi Therapeutics

Now known as Sierra Oncology, is a clinical stage drug development company in Vancouver that focuses on cancer and hematology treatments.

2

Funding Rounds

$71.5m

Money raised

Korro Bio logo

Korro Bio

Korro Bio is a biotechnology company based in Cambridge, Massachusetts focused on the research and development of RNA editing technology.

2

Funding Rounds

$207.5m

Money raised

Arrakis Therapeutics logo

Arrakis Therapeutics

Arrakis is developing RNA-targeted small molecule (rSM) therapies to millions of patients.

4

Funding Rounds

$226.0m

Money raised

Spark Therapeutics logo

Spark Therapeutics

Spark Therapeutics is a Philadelphia-based therapeutics and biotechnology company founded in 2013.

2

Funding Rounds

$122.8m

Money raised

Quark Pharmaceuticals logo

Quark Pharmaceuticals

Quark Pharmaceuticals is a RNAi-based, late stage clinical company founded in 2002 by Daniel Zurr.

1

Funding Rounds

$27.0m

Money raised

Stemirna Therapeutics logo

Stemirna Therapeutics

Stemirna Therapeutics is an mRNA therapeutics and nanoparticle formulation company in China focused on treatments for cancer, infectious diseases and rare diseases.

1

Funding Rounds

$14.2m

Money raised

DxTerity Diagnostics logo

DxTerity Diagnostics

DxTerity Diagnostics is a genomics company developing genomic tests for disease diagnosis and monitoring. Los Angeles-based company.

5

Funding Rounds

$4.1m

Money raised

Audentes Therapeutics logo

Audentes Therapeutics

Audentes Therapeutics is a San Francisco-based therapeutics and genetic medicines company.

3

Funding Rounds

$137.5m

Money raised

Triplet Therapeutics logo

Triplet Therapeutics

A therapeutics company developing siRNA and ASO therapeutics that target repeat expansion disorders such as Huntington’s disease, myotonic dystrophy and spinocerebellar ataxias

1

Funding Rounds

$59.0m

Money raised

OyaGen logo

OyaGen

OyaGen is an HIV Drug Discovery, Editing Enzymes founded in 2003 by Harold Smith.

5

Funding Rounds

$6.6m

Money raised

SeqLL logo

SeqLL

Seqll is a company providing quantitative RNA and specialty DNA sequencing services.

3

Funding Rounds

$3.0m

Money raised

Mirna Therapeutics logo

Mirna Therapeutics

A research and development company for miRNA-directed treatments for cancer and other diseases

2

Funding Rounds

$36.0m

Money raised

Locanabio logo

Locanabio

Locanabio is a San Diego, California-based biotechnology company developing RNA-targeting gene therapies.

4

Funding Rounds

$210.6m

Money raised

Spring Bank Pharmaceuticals, Inc. logo

Spring Bank Pharmaceuticals, Inc.

Spring Bank Pharmaceuticals, Inc. is a company founded in 2002

6

Funding Rounds

$49.6m

Money raised

Storm Therapeutics logo

Storm Therapeutics

Small molecule inhibitors of RNA-modifying enzymes for the treatment of cancer

4

Funding Rounds

$101.6m

Money raised

Biosplice Therapeutics logo

Biosplice Therapeutics

Small Molecules Acting on Stem Cells. Biosplice Therapeutics is in the medical research and development for tissue-level regeneration.

6

Funding Rounds

$799.0m

Money raised

Silence Therapeutics logo

Silence Therapeutics

Silence Therapeutics is a London-based company founded in 1999.

1

Funding Rounds

$45.5m

Money raised

Ribometrix logo

Ribometrix

Small molecule drugs that target functional 3D RNA structures to treat human diseases.

4

Funding Rounds

$52.8m

Money raised

Eclipse Bioinnovations logo

Eclipse Bioinnovations

Eclipse Bioinnovations is a San Diego-based company that develops RNA medicines.

2

Funding Rounds

$29.0m

Money raised

Advanced Cell Diagnostics logo

Advanced Cell Diagnostics

A company that provides cell and tissue based diagnostic tests for personalized medicine development

2

Funding Rounds

$17.4m

Money raised

Strand Therapeutics logo

Strand Therapeutics

Strand Therapeutics is a gene Therapy founded by Darrell Irvine, Jacob Becraft, Ron Weiss and Tasuku Kitada.

3

Funding Rounds

$103.1m

Money raised

Expansion Therapeutics logo

Expansion Therapeutics

Expansion Therapeutics is a RNA Targeted Small Molecules founded in 2016.

2

Funding Rounds

$135.3m

Money raised

Geneoscopy, Inc. logo

Geneoscopy, Inc.

Geneoscopy, Inc. is a St. Louis-based developer of medical diagnostics systems including non-invasive cancer diagnostics from biomarkers.

4

Funding Rounds

$126.7m

Money raised

Alithea Genomics logo

Alithea Genomics

Alithea Genomics backgrounds in bioengineering, molecular biology, genomics and lab operations reflect their complementary expertise.

2

Funding Rounds

$2.0m

Money raised

NanoCor Therapeutics logo

NanoCor Therapeutics

A biotechnology company developing intracellular genetic protein therapy to treat chronic heart failure

3

Funding Rounds

$17.6m

Money raised

Vico Therapeutics logo

Vico Therapeutics

Vico Therapeutics is a medicine for rare neurological diseases founded in 2019.

4

Funding Rounds

$179.0m

Money raised

Renova Therapeutics logo

Renova Therapeutics

Renova Therapeutics is a company that envisions a future where it can permanently treat chronic diseases

2

Funding Rounds

$7.5m

Money raised

RNAimmune, Inc. logo

RNAimmune, Inc.

RNAimmune is a biotechnology startup in the field of messenger RNA (mRNA) technology with more than 20 years’ expertise in handling and optimizing this versatile molecule for medical purposes.

3

Funding Rounds

$14.8m

Money raised

Orna Therapeutics logo

Orna Therapeutics

Orna Therapeutics is a biotechnology company dedicated to designing and delivering a new class of fully engineered circular RNA (oRNA) therapeutics.

2

Funding Rounds

$321.0m

Money raised

InteRNA Technologies logo

InteRNA Technologies

InteRNA Technologies is a biotech company.

5

Funding Rounds

$37.6m

Money raised

Skyhawk Therapeutics logo

Skyhawk Therapeutics

Skyhawk Therapeutics is a RNA-correcting Small Molecules founded in 2016 by Bill Haney.

2

Funding Rounds

$48.0m

Money raised

Mirvie logo

Mirvie

Mirvie is a biotech company that creates precise, actionable, and non-invasive tests for maternal-fetal health.Mirvie is a biotech company that creates precise, actionable, and non-invasive tests for maternal-fetal health.

1

Funding Rounds

$60.0m

Money raised

Abogen Biosciences logo

Abogen Biosciences

Abogen Biosciences is a China-based company.

4

Funding Rounds

$1.4b

Money raised

Agilis Biotherapeutics Inc. logo

Agilis Biotherapeutics Inc.

Agilis Biotherapeutics Inc. is a Cambridge, Massachusetts-based biotechnology company founded in 2013.

3

Funding Rounds

$36.3m

Money raised

Remix Therapeutics logo

Remix Therapeutics

Small molecule therapies designed to reprogram RNA processing

2

Funding Rounds

$151.0m

Money raised

Twentyeight-Seven Therapeutics logo

Twentyeight-Seven Therapeutics

Twentyeight-Seven is a biomedical startup with a passion for cutting-edge life saving technology.

1

Funding Rounds

$65.0m

Money raised

Amyl Therapeutics logo

Amyl Therapeutics

Amyl Therapeutics unique technology offers a curative solution for all forms of amyloid mediated diseases

3

Funding Rounds

$33.6m

Money raised

Ra Pharmaceuticals logo

Ra Pharmaceuticals

Ra Pharmaceuticals is a Cambridge, Massachusetts-based company.

1

Funding Rounds

$8.6m

Money raised

Immune Design logo

Immune Design

An immunotherapy company developing approaches to enable the body's immune system to fight against diseases

3

Funding Rounds

$99.0m

Money raised

Shape Therapeutics logo

Shape Therapeutics

Shape Therapeutics is a RNA-editing gene therapy.

2

Funding Rounds

$147.5m

Money raised

ImmusanT logo

ImmusanT

A biotechnology company developing therapies and personalized diagnostics for celiac disease

3

Funding Rounds

$60.0m

Money raised

HDT Bio Corp. logo

HDT Bio Corp.

HDT Bio Corp. is a RNA delivery technology, Immune Activators (Adjuvants.

1

Funding Rounds

$3.0m

Money raised

MiNA Therapeutics logo

MiNA Therapeutics

MiNA Therapeutics is a small activating RNA founded in 2008.

1

Funding Rounds

$23.0m

Money raised

Leyden Labs logo

Leyden Labs

Leyden Labs is a mucosal protection platform founded in 2020.

2

Funding Rounds

$187.1m

Money raised

PolyTherics logo

PolyTherics

A company developing biomedical polymers technology for therapeutic applications

2

Funding Rounds

$8.6m

Money raised

Regado Biosciences logo

Regado Biosciences

A company developing antithrombotic drug systems to treat acute and sub-acute cardiovascular and other indications

3

Funding Rounds

$114.0m

Money raised

Atox Bio logo

Atox Bio

A company developing immunomodulators to treat acute inflammatory conditions

2

Funding Rounds

$33.3m

Money raised

GenVec logo

GenVec

GenVec is a biopharmaceutical company developing therapeutics and vaccines founded in 1992.

1

Funding Rounds

$2.0m

Money raised

PhaseRx logo

PhaseRx

PhaseRx is a company developing macromolecular therapeutics to treat diseases.

1

Funding Rounds

$19.0m

Money raised

Promosome logo

Promosome

Promosome is a company developing technologies to regulate protein synthesis founded in 2003.

2

Funding Rounds

$13.7m

Money raised

Laronde logo

Laronde

Laronde is a plasmid RNA Therapeutics.

1

Funding Rounds

$440.0m

Money raised

RXi Pharmaceuticals logo

RXi Pharmaceuticals

RXi Pharmaceuticals is a company developing ribonucleic acid interference-based therapeutics founded in 2011.

1

Funding Rounds

$23.6m

Money raised

Resalis Therapeutics logo

Resalis Therapeutics

Resalis Therapeutics is developing first-in-class anti-miR compounds to address high unmet medical needs in liver diseases, metabolic disorders, and cancer using a multi-pathway approach.

1

Funding Rounds

$11.0m

Money raised

InDex Pharmaceuticals logo

InDex Pharmaceuticals

InDex Pharmaceuticals is a Stockholm-based company developing immunotherapy products.

1

Funding Rounds

$11.3m

Money raised

Cebix logo

Cebix

Cebix is a biopharmaceutical company developing treatments for diabetic complications founded in 2008.

2

Funding Rounds

$46.9m

Money raised

ADARx logo

ADARx

ADARx is developing a RNA targeting platform focused on genetic, cardiometabolic and central nervous system diseases

1

Funding Rounds

$75.0m

Money raised

Abcombi Biosciences logo

Abcombi Biosciences

Abcombi Biosciences is a company founded in 2015 by Andrew Hill, Ph.D. .

1

Funding Rounds

iTolerance logo

iTolerance

iTolerance is a Miami, Florida-based biotechnology company specializing in regenerative medicine without immunosuppression.

1

Funding Rounds

$20.0m

Money raised

Pangea Biomed logo

Pangea Biomed

A technology company with a focus on precision oncology solutions.

1

Funding Rounds

$7.0m

Money raised

Wobble Genomics logo

Wobble Genomics

Wobble Genomics specializes in maximizing RNA and DNA sequencing efficiency for the discovery and detection of nucleic acid biomarkers.

1

Funding Rounds

$11.0m

Money raised

Protai logo

Protai

Empowering drug discovery with Proteomics and ML to unlock complex biological insights and enable better therapeutics.

1

Funding Rounds

$8.0m

Money raised

Groove Biopharma. logo

Groove Biopharma.

Groove Biopharma. is a biotechnology company.

1

Funding Rounds

$6.0m

Money raised

Codetta Biosciences logo

Codetta Biosciences

Codetta Biosciences is a Morrisville, North Carolina-based company.

1

Funding Rounds

$15.0m

Money raised

Quris logo

Quris

Quris is an AI Drug Discovery.

1

Funding Rounds

$28.0m

Money raised

Vernal Biosciences logo

Vernal Biosciences

Vernal Biosciences is a mRNA Production founded in 2021 by Christian Cobaugh.

1

Funding Rounds

$21.0m

Money raised