2
Funding Rounds
$98.0m
Money raised
OrphAI Therapeutics is a biotechnology research company based in Guilford, Connecticut that develops precision therapeutics technology designed to treat cancer and rare diseases.
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Location:
3
Funding Rounds
$117.5m
Money raised
A biopharmaceutical company focused on developing treatments for urea cycle disorders and other rare diseases
5
Funding Rounds
$76.5m
Money raised
AllStripes is a U.S-based company offering a rare disease medical information database.
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Location:
4
Funding Rounds
$124.1m
Money raised
Healx is a biotechnology therapeutics company for rare diseases founded in 2014 by Tim Guilliams.
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Location:
Key people:
- David Brown *****.*****@healx.ai
- Tim Guilliams ***.*********@healx.ai
3
Funding Rounds
$250.0m
Money raised
Hemab Therapeutics is pioneering the first preventative treatments for rare bleeding and thrombotic disorders to ensure no patient is ever left behind
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Location:
2
Funding Rounds
$140.0m
Money raised
Disc Medicine is a medical research company that develops treatments for hematologic diseases.
Industries:
Key people:
1
Funding Rounds
$35.4m
Money raised
We are dedicated to improving the lives of patients suffering from hematological malignancies by delivering an innovative immune modulator to enhance the curative potential of allogeneic Hematopoietic Stem Cell Transplantation (HSCT).
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Location:
1
Funding Rounds
$40.0m
Money raised
Wilson Therapeutics is an every Day We Change Lives founded in 1992.
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Location:
13
Funding Rounds
$147.7m
Money raised
Minoryx Therapeutics is a small Molecules for Rare Diseases founded in 2011.
Location:
3
Funding Rounds
$88.3m
Money raised
CENTOGENE is a Rostock-based healthcare company developing methods and technologies for genetics analysis.
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Key people:
1
Funding Rounds
$3.9m
Money raised
We’re here to inspire an information revolution in rare disease. Our contribution will be to build a knowledge bank for the lived experience of rare disease, and it will catalog every aspect of life with a rare condition: specifically, any of the 7000+ rare conditions. Incredibly ambitious? You bet.
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Location:
2
Funding Rounds
$44.0m
Money raised
InnoSkel is a therapies for Rare Skeletal Diseases founded in 2020 by Elvire Gouze.
2
Funding Rounds
$50.9m
Money raised
Clinical stage treatment for Myotonic Dystrophy Type 1
1
Funding Rounds
$675.0k
Money raised
Mendelian Ltd is a London-based diagnostics company developing rare disease diagnostics.
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Location:
Key people:
- Fran Garcia ****@mendelian.co
- Ignacio Hernández Medrano
- Rudy Benfredj ****@mendelian.co
1
Funding Rounds
$50.0m
Money raised
Computational platform for small molecule discovery targeting protein misfolding diseases
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Location:
2
Funding Rounds
$100.0m
Money raised
Therachon is a company founded in 2014.
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Location:
1
Funding Rounds
$1.5m
Money raised
ThinkGenetic is a company founded in 2016 by Dave Jacob.
Industries:
Location:
Key people:
1
Funding Rounds
$27.5m
Money raised
Azafaros is a small Molecules.